American Gene Technolgies is devleoping therapeutics based on lentiviral vectors to target HIV, PKU, Liver cancer, Parkinson's disease, and familial dysautonomia.
BioBlast Pharma manufactures Trehalose, a therapeutic to potentially treat a number of devastating PolyA/PolyQ diseases. Trehalose acts as a chemical chaperone to protects against pathological ...
Fibrodysplasia ossificans progressiva treatments
Autism and Fragile X Syndrome treatments
Exemplar Genetics develops specialized miniature swine models that are genetically engineered to exhibit a wide variety of human disease states, to provide a more accurate platform to test the ...
Genomics Medicine Ireland is embarking on a multi-year, island-wide health discovery project which aims to build the largest, most comprehensive population-scale, disease-specific genomic study ...
KromaTiD, Inc. provides products and services for mutation detection and disease diagnosis. KromaTiD’s patented
Cystic Fibrosis treatment
NIPD Genetics designs, develops and provides advanced tests for the prediction, diagnosis and prevention of genetic diseases.