Akcea is developing treatments for unaddressed or under-addressed serious and rare diseases with leading-edge, RNA-targeted medicines.
Arcturus Therapeutics Ltd. is a preclinical-stage biopharmaceutical company primarily focused on the discovery, development and commercialization of RNA medicines using proprietary lipid-mediated ...
ARQ Genetics offers custom-designed gene panels to provide accurate real-time gene expression data.
Arrowhead Pharmaceuticals develops medicines that treat intractable diseases by silencing the genes that cause them. Using a broad portfolio of RNA chemistries and efficient modes of delivery, ...
BioNTech was founded in 2008 on the understanding that every cancer patient’s tumor is unique and therefore each patient’s treatment should be individualized. Its cutting-edge pipeline includes ...
Develops Enhanced CrossLinking and Immunoprecipitation (eCLIP), followed by high-throughput sequencing (eCLIP-seq), to identify RNA transcripts bound in vivo by a protein of interest.
mRNA based medicines for rare diseases
enGene Inc. has developed a highly flexible nucleotide (DNA and RNAi) delivery technology that targets mucosal tissues and can be used to treat numerous prevalent, chronic diseases via the ...
Ethris is paving a new path from genes to therapeutic proteins using our proprietary messenger RNA technologies. Their integrated platform enables the discovery, design and development of ...
Expansion Therapeutics is a drug discovery and development company pursuing the vast potential of small molecule medicines for RNA-mediated diseases.
Greenlight Biosciences uses a cell-free production platform to develop RNA products for plant and life science applications.
Multivalent RNAi Platform, Delivery
Ionis makes antisense oligonucletides that target mRNA molecules that code for toxic proteins.
Gene therapy requires delivery. Ligandal has developed a breakthrough nanotechnology for the precise and high-efficiency delivery of nucleic acids (CRISPR, TALEN, and RNA) to specific cells and ...
miRNA Oncology Therapies
Moderna is working on mRNA therapeutics and vaccines for infectious diseases, immuno-oncology, rare diseases and cardiovascular diseases.
RNA Profiling and Services