BioBlast Pharma

Website: BioBlast Pharma
Business Area(s): 


Description: 

BioBlast Pharma manufactures Trehalose, a therapeutic to potentially treat a number of devastating PolyA/PolyQ diseases. Trehalose acts as a chemical chaperone to protects against pathological processes in cells.  Trehalose reduces protein aggregation in several diseases associated with abnormal cellular-protein aggregation as well as acting as an autophagy enhancer. Trehalose 90 mg/mL IV solution has been documented as demonstrating significant promise in preclinical animal models of OPMD; spinocerebellar ataxia, type 3 (SCA3); and other PolyA/PolyQ diseases.

Location(s): 
New Haven CT
United States